Fitusiran, an experimental hemophilia therapy administered through a monthly subcutaneous injection, met its primary endpoint in a phase III trial being presented at the 63rd American Society of Hematology (ASH) Annual Meeting and Exposition. The drug dramatically reduced bleeding events, with half of those receiving it experiencing no bleeds and 85% experiencing an annualized bleed rate of three or fewer bleeds over the study period of about eight months. Dr. Alok Srivastava (Batch 1976) presented finds of this new study at the conference on December 14th, 2021. Read more here.
A boost in research and development will be the first step toward the elimination of these diseases. CMC Alumni Priscilla Rupalli (Batch 1987) and Winsley Rose (Batch 1991) discuss the